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Trial details imported from ClinicalTrials.gov

For full trial details, please see the original record at https://clinicaltrials.gov/study/NCT02051608




Registration number
NCT02051608
Ethics application status
Date submitted
30/01/2014
Date registered
31/01/2014
Date last updated
10/02/2023

Titles & IDs
Public title
A Study of Gantenerumab in Participants With Mild Alzheimer Disease
Scientific title
A Phase III, Randomized, Double-Blind, Placebo-Controlled, Parallel-Group, Multicenter, Efficacy and Safety Study of Gantenerumab in Patients With Mild Alzheimer's Disease; Part II: Open-Label Extension For Participating Patients
Secondary ID [1] 0 0
2013-003390-95
Secondary ID [2] 0 0
WN28745
Universal Trial Number (UTN)
Trial acronym
Linked study record

Health condition
Health condition(s) or problem(s) studied:
Alzheimer's Disease 0 0
Condition category
Condition code
Neurological 0 0 0 0
Alzheimer's disease
Neurological 0 0 0 0
Dementias

Intervention/exposure
Study type
Interventional
Description of intervention(s) / exposure
Treatment: Drugs - Placebo
Treatment: Drugs - Gantenerumab

Placebo comparator: Part 1 (Double Blind treatment): Placebo - Participants received matching placebo by subcutaneous (SC) injection every 4 weeks (Q4W) up to 100 weeks during Part 1 of the study.

Experimental: Part 1 (Double Blind treatment): Gantenerumab - Participants received 105 mg Gantenerumab by SC injection Q4W for 24 weeks and if eligible 225 mg SC injection Q4W from weeks 28-100 during Part 1 of the study.

Placebo comparator: Part 2 (Open-Label Extension [OLE] treatment): Placebo switched to Gantenerumab Up to 1200 mg - Participants who had received Placebo in Part 1, received Gantenerumab at doses up to 1200 mg by SC injection Q4W for up to 2 years. Additionally, participants were given the option to continue receiving open-label gantenerumab treatment for 3 years.

Experimental: Part 2 (OLE treatment): Gantenerumab up to 1200 mg - Participants who had received Gantenerumab in Part 1, received treatment at doses up to 1200 mg by SC injection Q4W for up to 2 years. Additionally, participants were given the option to continue receiving open-label gantenerumab treatment for 3 years.


Treatment: Drugs: Placebo
Participants received Placebo SC injection Q4W.

Treatment: Drugs: Gantenerumab
Participants received Gantenerumab at 105 mg , 225 mg, or at doses up to 1200 mg SC injection Q4W.

Intervention code [1] 0 0
Treatment: Drugs
Comparator / control treatment
Control group

Outcomes
Primary outcome [1] 0 0
Part 2: Percentage of Participants With Adverse Events (AEs) or Serious Adverse Events (SAEs)
Timepoint [1] 0 0
First dose up to 4 weeks after the last dose of study drug (up to 249 weeks)
Primary outcome [2] 0 0
Part 2: Percentage of Participants With Treatment Emergent Anti-Drug Antibodies (ADAs)
Timepoint [2] 0 0
First dose up to last dose (Baseline up to until maximum 5 years)
Primary outcome [3] 0 0
Part 2: Percentage of Participants With Adverse Events Leading to Discontinuation of Treatment
Timepoint [3] 0 0
First dose up to 4 weeks after the last dose in OLE (Up to approximately 249 weeks)
Secondary outcome [1] 0 0
Part 1: Percentage of Participants With AEs, SAEs
Timepoint [1] 0 0
First dose up to last dose (Up to approximately 152 weeks)
Secondary outcome [2] 0 0
Part 1: Percentage of Participants With Treatment Emergent ADAs
Timepoint [2] 0 0
First dose up to last dose (Up to approximately 152 weeks)
Secondary outcome [3] 0 0
Part 1: Gantenerumab Plasma Concentration at Multiple Timepoints
Timepoint [3] 0 0
Pre-dose: Weeks 4, 8, 12, 24, 48, 72 and Post dose: Day 4
Secondary outcome [4] 0 0
Part 1: Percentage of Participants With Adverse Events Leading to Discontinuation of Treatment
Timepoint [4] 0 0
First dose up to last dose (Up to approximately 152 weeks)
Secondary outcome [5] 0 0
Part 2: Percent Change From Baseline in Hippocampal Volume at Week 104
Timepoint [5] 0 0
Baseline (Part 1 screening), Week 104
Secondary outcome [6] 0 0
Part 2: Percent Change From Baseline in Whole Brain Volume at Week 104
Timepoint [6] 0 0
Baseline (Part 1 screening), Week 104
Secondary outcome [7] 0 0
Part 2: Percent Change From Baseline in Cortical Thickness at Week 104
Timepoint [7] 0 0
Baseline (Part 1 screening), Week 104
Secondary outcome [8] 0 0
Part 2: Ventricular Volume as Measured by MRI at Week 104
Timepoint [8] 0 0
Part 2: Week 104
Secondary outcome [9] 0 0
Part 2: Gantenerumab Plasma Concentration at Multiple Timepoints
Timepoint [9] 0 0
Pre-dose: Weeks 104, 116, 156, 208; Post-dose: Weeks 53, 101
Secondary outcome [10] 0 0
Part 2: Change From Baseline in Brain Amyloid Load at Week 156 in a Subset of Participants
Timepoint [10] 0 0
Baseline, Week 156

Eligibility
Key inclusion criteria
* Clinical diagnosis of probable mild Alzheimer disease (AD) based on National Institute of Neurological and Communicative Disorders and Stroke/Alzheimer's Disease and Related Disorders Association (NINCDS/ADRDA) criteria or major NCD based whether or not receiving AD approved medication
* Cerebral spinal fluid (CSF) result consistent with the presence of amyloid pathology
* Availability of a person ('caregiver') who in the investigator's judgment has frequent and sufficient contact with the participant, and is able to provide accurate information regarding the participant's cognitive and functional abilities
* Fluency in the language of the tests used at the study site
* Willingness and ability to complete all aspects of the study
* Adequate visual and auditory acuity, in the investigator's judgment, sufficient to perform the neuropsychological testing (eye glasses and hearing aids are permitted)
* If currently receiving approved medications for AD, the dosing regimen must have been stable for 3 months prior to screening
* Agreement not to participate in other research studies for the duration of this trial and its associated substudies

PART 2 - All participants who have been randomized and are actively participating in the study are eligible for Part 2
Minimum age
50 Years
Maximum age
90 Years
Sex
Both males and females
Can healthy volunteers participate?
No
Key exclusion criteria
* Dementia or neurocognitive disorder (NCD) due to a condition other than AD, including, but not limited to, frontotemporal dementia, Parkinson disease, dementia with Lewy bodies, Huntington disease, or vascular dementia
* History or presence of clinically evident vascular disease potentially affecting the brain that in the opinion of the investigator has the potential to affect cognitive function
* History or presence of stroke within the past 2 years or documented history of transient ischemic attack within the last 12 months
* History or presence of systemic autoimmune disorders potentially causing progressive neurologic disease with associated cognitive deficits
* History of schizophrenia, schizoaffective disorder, or bipolar disorder
* Alcohol and/or substance use disorder (according to the DSM-5) within the past 2 years (nicotine use is allowed)
* History or presence of atrial fibrillation
* Within the last 2 years, unstable or clinically significant cardiovascular disease (e.g., myocardial infarction, angina pectoris, cardiac failure New York Heart Association Class II or higher)
* Uncontrolled hypertension
* Chronic kidney disease
* Impaired hepatic function

PET imaging substudy, in addition to above:

- Prior participation in other research study or clinical care within the last year such that the total radiation exposure would exceed the local or national annual limits

Part 2 Participants who have been discontinued from the study

Study design
Purpose of the study
Treatment
Allocation to intervention
Randomised controlled trial
Procedure for enrolling a subject and allocating the treatment (allocation concealment procedures)
Methods used to generate the sequence in which subjects will be randomised (sequence generation)
Masking / blinding
Blinded (masking used)
Who is / are masked / blinded?
The people receiving the treatment/s


The people analysing the results/data
Intervention assignment
Parallel
Other design features
Phase
Phase 3
Type of endpoint/s
Statistical methods / analysis

Recruitment
Recruitment status
Completed
Data analysis
Reason for early stopping/withdrawal
Other reasons
Date of first participant enrolment
Anticipated
Actual
Date of last participant enrolment
Anticipated
Actual
Date of last data collection
Anticipated
Actual
Sample size
Target
Accrual to date
Final
Recruitment in Australia
Recruitment state(s)
SA,VIC,WA
Recruitment hospital [1] 0 0
Royal Adelaide Hospital; Memory Trials Centre - Adelaide
Recruitment hospital [2] 0 0
The Queen Elizabeth Hospital; Neurology - Woodville
Recruitment hospital [3] 0 0
Heidelberg Repatriation Hospital; Medical and Cognitive Research Centre - Heidelberg West
Recruitment hospital [4] 0 0
Australian Alzheimer's Research Foundation - Nedlands
Recruitment postcode(s) [1] 0 0
5000 - Adelaide
Recruitment postcode(s) [2] 0 0
5011 - Woodville
Recruitment postcode(s) [3] 0 0
3081 - Heidelberg West
Recruitment postcode(s) [4] 0 0
6009 - Nedlands
Recruitment outside Australia
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United States of America
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Arizona
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California
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Florida
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Indiana
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Louisiana
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Michigan
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Missouri
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New Jersey
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New York
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North Carolina
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Oklahoma
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Pennsylvania
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Rhode Island
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Tennessee
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Texas
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United States of America
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Utah
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Argentina
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Ciudad Autonoma Buenos Aires
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Bruxelles
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Belgium
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Leuven
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Sofia
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Varna
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Rennes
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Leipzig
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Germany
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Muenchen
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Germany
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Ulm
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Germany
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Incheon
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Manchester
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Preston
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United Kingdom
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Sheffield

Funding & Sponsors
Primary sponsor type
Commercial sector/industry
Name
Hoffmann-La Roche
Address
Country

Ethics approval
Ethics application status

Summary
Brief summary
Trial website
Trial related presentations / publications
Public notes

Contacts
Principal investigator
Name 0 0
Clinical Trials
Address 0 0
Hoffmann-La Roche
Country 0 0
Phone 0 0
Fax 0 0
Email 0 0
Contact person for public queries
Name 0 0
Address 0 0
Country 0 0
Phone 0 0
Fax 0 0
Email 0 0
Contact person for scientific queries

No information has been provided regarding IPD availability


What supporting documents are/will be available?

Results publications and other study-related documents

No documents have been uploaded by study researchers.